By Ben Hirschler | Jan 03, 2013 10:09 AM EST
The Western world's first drug to fix faulty genes promises to transform the lives of patients with an ultra-rare disease that clogs their blood with fat.
By Ben Hirschler | Nov 02, 2012 10:30 AM EDT
European officials have approved the Western world's first gene therapy drug in a milestone for the novel medical technology that fixes faulty genes.